研飞ivySCI (青藤学术）

Molecular Therapy Methods and Clinical Development

短名	Mol. Ther. Methods Clin. Dev.
Journal Impact	4.43
国际分区	MEDICINE, RESEARCH & EXPERIMENTAL(Q2)
期刊索引	SCI Q2中科院 2 区

ISSN	2329-0501
h-index	60
国内分区	医学(2区)医学医学研究与实验(2区)

MOLECULAR THERAPY—METHODS & CLINICAL DEVELOPMENT 的目的是建立在 MOLECULAR THERAPY 在出版重要的同行评审方法和程序方面的成功的基础上，以及在分子治疗伞下广泛领域的转化进展。特别感兴趣的主题该期刊的范围包括：基因载体工程和生产、靶向基因组编辑和工程方法、细胞重编程和多能细胞定向分化的方法和技术开发、基因和细胞载体传递方法、生物材料和纳米粒子的开发在基因和细胞治疗和再生医学中的应用，基因和细胞载体的生物分布和追踪分析，新和下一代载体的药理学/毒理学研究，细胞分离、工程、培养、扩增和移植的方法，细胞加工、储存, 和银行用于治疗应用、临床前和 QC/QA 检测开发LOPMENT，转化和临床放大和良好制造程序和工艺开发，临床方案开发，用于分析、建模或生物数据可视化的计算和生物信息学方法，协商监管批准过程并获得此类临床试验批准。

期刊主页投稿网址

涉及主题	生物遗传学化学生物化学医学基因内科学免疫学细胞生物学遗传增强重组DNA病理病毒学细胞培养内分泌学分子生物学植物免疫系统心理学物理载体（分子生物学）癌症研究病毒病毒载体
出版信息	出版商: Cell Press，出版周期: ，期刊类型: journal
基本数据	创刊年份: 2014，原创研究文献占比: 94.59%，自引率:N.A.， Gold OA占比: 90.58%
平均审稿周期	网友分享经验：12 Weeks

期刊引文格式

这些示例是对学术期刊文章的引用，以及它们应该如何出现在您的参考文献中。

并非所有期刊都按卷和期组织其已发表的文章，因此这些字段是可选的。有些电子期刊不提供页面范围，而是列出文章标识符。在这种情况下，使用文章标识符而不是页面范围是安全的。

只有1位作者的期刊

有2位作者的期刊

有3位作者的期刊

有5位以上作者的期刊

书籍引用格式

以下是创作和编辑的书籍的参考文献的示例。

学位论文引用格式

网页引用格式

这些示例是对网页的引用，以及它们应该如何出现在您的参考文献中。

专利引用格式

An HPLC-SEC-based rapid quantification method for vesicular stomatitis virus particles to facilitate process development

2024-9-12

Preclinical development of hematopoietic stem cell-gene therapy for Mucopolysaccharidosis type IVB using a GLB1 transgene with enhanced therapeutic potential.

2024-9-1

Treating late-onset Tay Sachs disease: Brain delivery with a dual trojan horse protein

2024-9-1

Characterization of residual microRNAs in AAV vector batches produced in HEK293 mammalian cells and Sf9 insect cells

2024-9-1

DNA Contamination Within Recombinant Adeno Associated Virus (AAV) Preparations Correlates with Decreased CD34+ Cell Clonogenic Potential

2024-9-1

Subacute liver injury in two young infants following gene replacement therapy for spinal muscular atrophy

2024-9-1

Assessment of adeno-associated virus purity by capillary electrophoresis-based western

2024-9-1

A self-complementary AAV proviral plasmid that reduces cross-packaging and ITR promoter activity in AAV vector preparations

2024-9-1

Persistent tailoring of MSC activation through genetic priming

2024-9-1

Combination AAV Gene Therapy with Galectin-1 and SOD1 Downregulation Demonstrates Superior Therapeutic Effect in a severe mouse model of ALS

2024-9-1

Optimal different adeno-associated virus capsid/promoter combinations to target specific cell types in the common marmoset cerebral cortex

2024-9-1

Atelocollagen supports three-dimensional culture of human induced pluripotent stem cells

2024-9-1

Gene Therapy and kidney diseases

2024-9-1

A randomized, double-blind phase 2b trial to evaluate efficacy of ChAd63-KH for treatment of post kala-azar dermal leishmaniasis

2024-9-1

An autonucleolytic suspension HEK293F host cell line for high-titre serum-free AAV5 and AAV9 production with reduced levels of DNA impurity

2024-9-1

Evaluation of a rapid multi-attribute combinatorial high-throughput UV-Vis/DLS/SLS analytical platform for rAAV quantification and characterization

2024-9-1

Assessment of Adeno-Associated Virus Purity by Capillary Electrophoresis-Based Western

2024-9-1

Probing recombinant AAV capsid integrity and genome release after thermal stress by mass photometry

2024-9-1

Protein is expressed in all major organs after intravenous infusion of mRNA-lipid nanoparticles in swine

2024-9-1

A pseudotyped adenovirus serotype 5 vector with serotype 49 fiber knob is an effective vector for vaccine and gene therapy applications

2024-9-1

Resolving hidden subpopulations of filled AAVs by probing capsid integrity

2024-8-29

Production of Recombinant Adeno-associated Virus 5 Using a Novel Self-Attenuating Adenovirus Production Platform

2024-8-14

Auto-expansion of in vivo HDAd-transduced hematopoietic stem cells by constitutive expression of tHMGA2

2024-8-13

Validation of high-sensitivity fluorometric assays to quantitate cerebrospinal fluid and serum β-galactosidase activity in patients with GM1-gangliosidosis

2024-8-10

Lentiviral vector packaging and producer cell lines yield titres equivalent to the industry-standard four-plasmid process Stable cells for lentiviral vector manufacturing

2024-8-8

A Novel Approach to Quantitate In Vivo Biodistribution and Transduction of Adeno-Associated Viral Based Gene Therapy Using Iodine-125 and Indium-111-Labeled AAV Vector in Mice

2024-8-1

Longitudinal characterization of sub-retinal pigment epithelium deposit formation in a primary porcine tissue culture model of dry age-related macular degeneration

2024-8-1

Quantification of circulating TCR-engineered T cells targeting a human endogenous retrovirus post-adoptive transfer using nanoplate digital PCR

2024-8-1

Unlocking DOE potential selecting the most appropriate design for rAAV optimization

2024-8-1

Predictive power of deleterious single amino acid changes to infer on AAV2 and AAV2-13 capsids fitness

2024-8-1

A cellular disease model toward gene therapy of TGM1-dependent lamellar ichthyosis

2024-8-1

Lipid nanoparticle encapsulation improves effectiveness of a Delta Spike-CD40L DNA vaccine against homologous and heterologous SARS-CoV-2 challenge in Syrian hamsters

2024-8-1

CRISPR-Cas9-mediated genome editing delivered by a single AAV9 vector inhibits HSV-1 reactivation in a latent rabbit keratitis model

2024-8-1

Linker-specific monoclonal antibodies present a simple and reliable detection method for scFv-based CAR-NK cells

2024-8-1

Synergy between Lactobacillus murinus and anti-PcrV antibody delivered in the airways to promote protection against Pseudomonas aeruginosa

2024-8-1

Macrophage manufacturing and engineering with 5′-Cap1 and N1-methylpseudouridine-modified mRNA

2024-7-31

Characterization of AAV vectors: A review of analytical techniques and critical quality attributes

2024-7-30

Bio-Layer Interferometry for Adeno-Associated Virus Capsid Titer Measurement and Applications to Upstream and Downstream Process Development

2024-7-26

Modulation of the pharmacokinetics of soluble ACE2 decoy receptors through glycosylation

2024-7-19

Toward a large-batch manufacturing process for silicon-stabilized lipid nanoparticles: A highly customizable RNA delivery platform

2024-7-17

An amplification-free CRISPR/Cas12a assay for titer determination and composition analysis of the rAAV genome

2024-7-1

DNA-PK inhibition enhances gene editing efficiency in HSPCs for CRISPR-based treatment of X-linked hyper IgM syndrome

2024-7-1

The longitudinal kinetics of AAV5 vector integration profiles and evaluation of clonal expansion in mice

2024-6-26

Lipid nanoparticle-encapsulated DOCK11-siRNA efficiently reduces hepatitis B virus cccDNA level in infected mice

2024-6-24

5′ transgenes drive leaky expression of 3′ transgenes in Cre-inducible bicistronic vectors

2024-6-24

Highly Branched Poly β-amino ester/CpG-depleted CFTR Plasmid Nanoparticles for Non-viral Gene Therapy in Lung Cystic Fibrosis Disease

2024-6-24

Engineering single-cycle MeV vector for CRISPR/Cas9 gene editing

2024-6-24

Quantification of Full and Empty Particles of Adeno-Associated Virus Vectors via a Novel Dual Fluorescence-Linked Immunosorbent Assay

2024-6-24

Evaluation of anti-vector immune responses to adenovirus mediated lung gene therapy and modulation by αCD20

2024-6-24

Author’s full names, departments, institutions

2024-6-22

帮你贴心管理全部的文献
研飞ivySCI，高效的论文管理

投稿经验分享

分享我的经验，帮你走得更远

Molecular Therapy Methods and Clinical Development

期刊引文格式

只有1位作者的期刊

有2位作者的期刊

有3位作者的期刊

有5位以上作者的期刊

书籍引用格式

学位论文引用格式

网页引用格式

专利引用格式

最新文章

An HPLC-SEC-based rapid quantification method for vesicular stomatitis virus particles to facilitate process development

Preclinical development of hematopoietic stem cell-gene therapy for Mucopolysaccharidosis type IVB using a GLB1 transgene with enhanced therapeutic potential.

Treating late-onset Tay Sachs disease: Brain delivery with a dual trojan horse protein

Characterization of residual microRNAs in AAV vector batches produced in HEK293 mammalian cells and Sf9 insect cells

DNA Contamination Within Recombinant Adeno Associated Virus (AAV) Preparations Correlates with Decreased CD34+ Cell Clonogenic Potential

Subacute liver injury in two young infants following gene replacement therapy for spinal muscular atrophy

Assessment of adeno-associated virus purity by capillary electrophoresis-based western

A self-complementary AAV proviral plasmid that reduces cross-packaging and ITR promoter activity in AAV vector preparations

Persistent tailoring of MSC activation through genetic priming

Combination AAV Gene Therapy with Galectin-1 and SOD1 Downregulation Demonstrates Superior Therapeutic Effect in a severe mouse model of ALS

Optimal different adeno-associated virus capsid/promoter combinations to target specific cell types in the common marmoset cerebral cortex

Atelocollagen supports three-dimensional culture of human induced pluripotent stem cells

Gene Therapy and kidney diseases

A randomized, double-blind phase 2b trial to evaluate efficacy of ChAd63-KH for treatment of post kala-azar dermal leishmaniasis

An autonucleolytic suspension HEK293F host cell line for high-titre serum-free AAV5 and AAV9 production with reduced levels of DNA impurity

Evaluation of a rapid multi-attribute combinatorial high-throughput UV-Vis/DLS/SLS analytical platform for rAAV quantification and characterization

Assessment of Adeno-Associated Virus Purity by Capillary Electrophoresis-Based Western

Probing recombinant AAV capsid integrity and genome release after thermal stress by mass photometry

Protein is expressed in all major organs after intravenous infusion of mRNA-lipid nanoparticles in swine

A pseudotyped adenovirus serotype 5 vector with serotype 49 fiber knob is an effective vector for vaccine and gene therapy applications

Resolving hidden subpopulations of filled AAVs by probing capsid integrity

Production of Recombinant Adeno-associated Virus 5 Using a Novel Self-Attenuating Adenovirus Production Platform

Auto-expansion of in vivo HDAd-transduced hematopoietic stem cells by constitutive expression of tHMGA2

Validation of high-sensitivity fluorometric assays to quantitate cerebrospinal fluid and serum β-galactosidase activity in patients with GM1-gangliosidosis

Lentiviral vector packaging and producer cell lines yield titres equivalent to the industry-standard four-plasmid process Stable cells for lentiviral vector manufacturing

A Novel Approach to Quantitate In Vivo Biodistribution and Transduction of Adeno-Associated Viral Based Gene Therapy Using Iodine-125 and Indium-111-Labeled AAV Vector in Mice

Longitudinal characterization of sub-retinal pigment epithelium deposit formation in a primary porcine tissue culture model of dry age-related macular degeneration

Quantification of circulating TCR-engineered T cells targeting a human endogenous retrovirus post-adoptive transfer using nanoplate digital PCR

Unlocking DOE potential selecting the most appropriate design for rAAV optimization

Predictive power of deleterious single amino acid changes to infer on AAV2 and AAV2-13 capsids fitness

A cellular disease model toward gene therapy of TGM1-dependent lamellar ichthyosis

Lipid nanoparticle encapsulation improves effectiveness of a Delta Spike-CD40L DNA vaccine against homologous and heterologous SARS-CoV-2 challenge in Syrian hamsters

CRISPR-Cas9-mediated genome editing delivered by a single AAV9 vector inhibits HSV-1 reactivation in a latent rabbit keratitis model

Linker-specific monoclonal antibodies present a simple and reliable detection method for scFv-based CAR-NK cells

Synergy between Lactobacillus murinus and anti-PcrV antibody delivered in the airways to promote protection against Pseudomonas aeruginosa

Macrophage manufacturing and engineering with 5′-Cap1 and N1-methylpseudouridine-modified mRNA

Characterization of AAV vectors: A review of analytical techniques and critical quality attributes

Bio-Layer Interferometry for Adeno-Associated Virus Capsid Titer Measurement and Applications to Upstream and Downstream Process Development

Modulation of the pharmacokinetics of soluble ACE2 decoy receptors through glycosylation

Toward a large-batch manufacturing process for silicon-stabilized lipid nanoparticles: A highly customizable RNA delivery platform

An amplification-free CRISPR/Cas12a assay for titer determination and composition analysis of the rAAV genome

DNA-PK inhibition enhances gene editing efficiency in HSPCs for CRISPR-based treatment of X-linked hyper IgM syndrome

The longitudinal kinetics of AAV5 vector integration profiles and evaluation of clonal expansion in mice

Lipid nanoparticle-encapsulated DOCK11-siRNA efficiently reduces hepatitis B virus cccDNA level in infected mice

5′ transgenes drive leaky expression of 3′ transgenes in Cre-inducible bicistronic vectors

Highly Branched Poly β-amino ester/CpG-depleted CFTR Plasmid Nanoparticles for Non-viral Gene Therapy in Lung Cystic Fibrosis Disease

Engineering single-cycle MeV vector for CRISPR/Cas9 gene editing

Quantification of Full and Empty Particles of Adeno-Associated Virus Vectors via a Novel Dual Fluorescence-Linked Immunosorbent Assay

Evaluation of anti-vector immune responses to adenovirus mediated lung gene therapy and modulation by αCD20

Author’s full names, departments, institutions

帮你贴心管理全部的文献.css-5myebc{font-size:14px;font-weight:var(--chakra-fontWeights-normal);margin-top:var(--chakra-space-1);margin-bottom:var(--chakra-space-1);}研飞ivySCI，高效的论文管理

帮你贴心管理全部的文献
研飞ivySCI，高效的论文管理